Balancing Nonsense Mutation Readthrough and Toxicity of Designer Aminoglycosides for Treatment of Genetic Diseases

S Guchhait, A Khononov, T Pienko, V Belakhov, T Baasov

Research output: Contribution to journalArticlepeer-review

1 Scopus citations
Original languageAmerican English
Pages (from-to)794-801
Number of pages8
JournalACS Medicinal Chemistry Letters
Volume14
Issue number6
DOIs
StatePublished - 27 Apr 2023

Keywords

  • &nbsp
  • Aminoglycosides
  • Cystic fibrosis
  • Genetic diseases
  • Nonsense mutations
  • Translational readthrough

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